First infusions with #Golodirsen #orphan medicine from Regional reimbursement for #DMDpatients in #Almaty, #Kazakhstan.

Next month plan to initiate treatment with #Casimersen. All #exonskippingtherapies in world are available for our patients.
#rarediseasecompanykazakhstan #businessdevelopmentinkazakhstan #CentralAsia #SareptaTherapeutics #orphandiseasepatientsinKazakhstan #orphanpharmaceuticalcompanyinKazakhstan #rarediseasepatientsinCentralAsia #orphanpharmacompany